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SMC ID Date Medicine Submission Type Indication
SMC2649 12/08/2024 etranacogene dezaparvovec (Hemgenix) Full

For treatment of severe and moderately severe haemophilia B (congenital Factor IX deficiency) in adult patients without a history of Factor IX inhibitors.
Publication due date SMC meeting date Medicine Submission Type Indication
TBC TBC marstacimab (Hympavzi) Full

For routine prophylaxis of bleeding episodes in patients 12 years of age and older, weighing at least 35 kg, with:

  • severe haemophilia A (congenital factor VIII deficiency, FVIII < 1%)
    without factor VIII inhibitors, or
  • severe haemophilia B (congenital factor IX deficiency, FIX < 1%) without
    factor IX inhibitors