Ultra Orphan Assessment
Treatment of patients with molybdenum cofactor deficiency (MoCD) Type A.
Medicine details
- Medicine name:
- fosdenopterin (Nulibry)
- SMC ID:
- SMC2624
- Pharmaceutical company
- Sentynl Therapeutics
- BNF chapter
- Nutrition and blood
- Submission type
- Ultra-orphan initial assessment
- Publication due date:
- 13 January 2025
- SMC meeting date:
- 06 August 2024
- Patient group submission deadline:
- 01 July 2024