Indication

Paroxysmal nocturnal hemoglobinuria (PNH), who have haemolytic anaemia.

Medicine details

Medicine name:
iptacopan (Fabhalta)
SMC ID:
SMC2676
Pharmaceutical company
Novartis Pharmaceuticals UK Ltd
BNF chapter
Nutrition and blood
Submission type
Full
Publication due date:
TBC
SMC meeting date:
TBC
Patient group submission deadline:
TBC