Advice
Following a resubmission.
Laronidase is not recommended for use within NHS Scotland for the treatment of mucopolysaccharidosis I. Laronidase was approved by the EMEA under exceptional circumstances and has been granted orphan drug status. No information is presented in the submission to support the therapy being cost effective.
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Medicine details
- Medicine name:
- Laronidase (Aldurazyme®)
- SMC ID:
- 100/04
- Indication:
- Mucopolysaccharidosis I
- Pharmaceutical company
- Genzyme Therapeutics Ltd
- BNF chapter
- Nutrition and blood
- Submission type
- Resubmission
- Status
- Not recommended
- Date advice published
- 13 December 2004