Advice

Following a full submission.

Miglustat is accepted for use within NHS Scotland for the treatment of mild to moderate type 1 Gaucher disease in patients for whom enzyme replacement therapy is unsuitable.

Miglustat should only be initiated by physicians experienced in the management of Gaucher’s disease.

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Medicine details

Medicine name:
Miglustat (Zavesca®)
SMC ID:
133/04
Indication:
Moderate type 1 Gaucher disease
Pharmaceutical company
Actelion Pharmaceuticals UK Ltd
BNF chapter
Nutrition and blood
Submission type
Full
Status
Accepted
Date advice published
13 December 2004