Advice

in the absence of a submission from the holder of the marketing authorisation:

nitisinone (Orfadin®) is not recommended for use within NHSScotland.

Indication under review: Treatment of adult patients with alkaptonuria (AKU).

The holder of the marketing authorisation has not made a submission to SMC regarding this product in this indication. As a result we cannot recommend its use within NHSScotland.

Download detailed advice614KB (PDF)

Download

Medicine details

Medicine name:
nitisinone (Orfadin)
SMC ID:
SMC2450
Indication:

Treatment of adult patients with alkaptonuria (AKU).

Pharmaceutical company
Swedish Orphan Biovitrum
BNF chapter
Nutrition and blood
Submission type
Non submission
Status
Not recommended
Date advice published
13 December 2021