Advice
in the absence of a submission from the holder of the marketing authorisation:
nitisinone (Orfadin®) is not recommended for use within NHSScotland.
Indication under review: Treatment of adult patients with alkaptonuria (AKU).
The holder of the marketing authorisation has not made a submission to SMC regarding this product in this indication. As a result we cannot recommend its use within NHSScotland.
Download detailed advice614KB (PDF)
Medicine details
- Medicine name:
- nitisinone (Orfadin)
- SMC ID:
- SMC2450
- Indication:
Treatment of adult patients with alkaptonuria (AKU).
- Pharmaceutical company
- Swedish Orphan Biovitrum
- BNF chapter
- Nutrition and blood
- Submission type
- Non submission
- Status
- Not recommended
- Date advice published
- 13 December 2021