Indication

For treatment of 5q spinal muscular atrophy (SMA).

Medicine details

Medicine name:
nusinersen (Spinraza)
SMC ID:
SMC2805
Pharmaceutical company
Biogen Idec Ltd
BNF chapter
Musculoskeletal and joint diseases
Submission type
Ultra-orphan reassessment
Publication due date:
TBC
SMC meeting date:
TBC
Patient group submission deadline:
TBC