Advice

in the absence of a submission from the holder of the marketing authorisation:

pegzilarginase (Loargys)®) is not recommended for use within NHSScotland.

Indication under review: treatment of arginase 1 deficiency (ARG1-D), also known as hyperargininemia, in adults, adolescents and children aged 2 years and older.

The holder of the marketing authorisation has not made a submission to SMC regarding this product in this indication.

As a result, we cannot recommend its use within NHSScotland.

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Medicine details

Medicine name:
pegzilarginase (Loargys)
SMC ID:
SMC2813
Indication:

Treatment of arginase 1 deficiency (ARG1-D), also known as hyperargininemia, in adults, adolescents and children aged 2 years and older.

Pharmaceutical company
Immedica
BNF chapter
Nutrition and blood
Submission type
Non submission
Status
Not recommended
Date advice published
09 June 2025