Advice

following a full submission assessed under the end of life and orphan process:

pemigatinib (Pemazyre®) is accepted for use within NHSScotland.

Indication under review: for the treatment of adults with locally advanced or metastatic cholangiocarcinoma with a fibroblast growth factor receptor 2 (FGFR2) fusion or rearrangement that have progressed after at least one prior line of systemic therapy.

In a phase II, single-arm study, pemigatinib demonstrated anti-tumour activity in patients with advanced/metastatic or surgically unresectable cholangiocarcinoma with a FGFR2 fusion or rearrangement who have progressed on at least one line of prior systemic therapy.

This advice applies only in the context of approved NHSScotland Patient Access Scheme (PAS) arrangements delivering the cost-effectiveness results upon which the decision was based, or PAS/ list prices that are equivalent or lower.

This advice takes account of the views from a Patient and Clinician Engagement (PACE) meeting.

Medicine details

Medicine name:
pemigatinib (Pemazyre)
SMC ID:
SMC2399
Indication:

As monotherapy for the treatment of adults with locally advanced or metastatic cholangiocarcinoma (CCA) with a fibroblast growth factor receptor 2 (FGFR2) gene fusion or rearrangement that have progressed after at least one prior line of systemic therapy.

Pharmaceutical company
Incyte Biosciences UK Ltd
BNF chapter
Malignant disease and immunosuppression
Submission type
Full
Status
Accepted
Date advice published
07 February 2022