Advice

following a full submission:

romiplostim (Nplate) is accepted for restricted use within NHSScotland for adult chronic immune (idiopathic) thrombocytopenic purpura (ITP) splenectomised patients who are refractory to other treatments (e.g. corticosteroids, immunoglobulins). Romiplostim is also accepted for restricted use as second line treatment for adult non-splenectomised patients where surgery is contra-indicated. Romiplostim is restricted to use in patients with severe symptomatic ITP or patients with a high risk of bleeding.

Romiplostim was significantly better than placebo in maintaining platelets at (or above) a minimum target level in previously treated patients with ITP.

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Medicine details

Medicine name:
romiplostim (Nplate)
SMC ID:
553/09
Indication:
Idiopathic (immune) thrombocytopenic purpura (ITP)
Pharmaceutical company
Amgen Ltd
BNF chapter
Nutrition and blood
Submission type
Full
Status
Restricted
Date advice published
12 October 2009
Additional notes

The marketing authorisation for romiplostim was extended to include use in adult non-splenectomised patients where surgery is not contra-indicated in January 2016. This minor licence change will not be assessed. The restriction to use in patients with severe symptomatic ITP or a high risk of bleeding still applies regardless of spleen status.