Indication

Treatment of 5q spinal muscular atrophy (Pre-symptomatic infants).

Medicine details

Medicine name:
nusinersen (Spinraza)
SMC ID:
SMC2877
Pharmaceutical company
Biogen
BNF chapter
Musculoskeletal and joint diseases
Submission type
Full
Publication due date:
TBC
SMC meeting date:
TBC
Patient group submission deadline:
01 June 2026